At the heart of our company is the belief that exceptional science and compassion are not mutually exclusive. We aim to develop life-changing treatments across a broad range of diseases through courageous science, a deep commitment to patients, and creativity to deliver meaningful outcomes. In order to make the biggest impact, our goal is to be representative of the patient, caregiver, and community voice.

By collaborating with patients, caregivers, and patient advocacy groups (PAGs), we strive to understand the experiences, opinions, and concerns of the community and embed these perspectives into our business decisions from clinical development to commercialization. Our goal is to design clinical trials, therapies, and resources that are representative of the communities we serve. We deeply value the partnerships and collaborations with PAGs, patients, and caregivers, and are committed to a continuous and transparent dialogue.

Click below to learn more about our areas of scientific focus.

Roger, living with PNH